Case Studies
Real programs. Real families. Real results.
Retinal Disease ASO Program
Section: Case Study Detail
Challenge
Family spent 2+ years navigating specialists, research labs, and conflicting opinions with no clear path forward after their daughter's Usher syndrome diagnosis.
Nome's Role
AI-powered therapeutic strategy, bespoke development blueprint, competitive RFP across commercial and academic partners, and turnkey execution to contracted SOW.
Result
From first contact to experiments underway in ~60 days — a 95% reduction in time to start a personalized medicine program.
What would have taken us years, they helped us accomplish in months.
Section: Additional Case Studies
Additional case studies will be added as programs progress across inherited retinal diseases and pediatric neurology.