Nome is for patients with genetic diseases and their care teams when there is no standard of care treatment option. We focus on conditions that are too rare for traditional pharmaceutical companies to address. If you have a confirmed genetic diagnosis and existing treatments haven't worked or don't exist, Nome might be able to help.

Safety is our top priority. Before any therapy reaches a patient, it must pass rigorous laboratory safety tests and receive permission from the FDA through an IND (Investigational New Drug) application. The FDA reviews all safety data before approving the first dose. During treatment, your medical team monitors every single dose, tracking how your body responds to ensure ongoing safety. While we cannot guarantee safety, we take maximum precaution at each step and we commit to transparently share potential risks with you in advance of receiving treatment and throughout your treatment journey.

We cannot guarantee that any experimental therapy will work for a patient. What we can promise is that we'll use the best available science, the most experienced experts, and work around the clock to provide the best possible chance of success, and we will be transparent about both the possibilities and limitations, helping you make an informed decision with your medical team.

We act as your concierge team at every step of the process. We have developed cutting edge AI tools that allow our experts to provide the right guidance at the lowest possible cost while maintaining high quality. We select the right partners required to execute on development, testing, and manufacturing of your therapy and manage their progress on your behalf. When a treatment is ready, we support the regulatory filing and clinical approval process. In short, we make action simple for the families who want our help.

After our initial evaluation, we can develop a comprehensive therapeutic plan in just 30 days. The total timeline to develop a therapy depends on your specific situation, but our technology and automation dramatically accelerate every step compared to traditional approaches. We know time is precious—many families don't have months or years to wait—so efficiency is built into everything we do.

We believe cost shouldn't be a barrier to getting started. Our initial report is completely free. We analyze your genetic data and provide guidance on whether a custom therapy might help. If you decide to proceed, we have transparent pricing for our services to develop your therapeutic plan and manage your program. While developing a personalized therapy is a costly process, we use technology and partnerships to significantly reduce that cost. As a patient-led organization, we understand how important it is to advance your therapeutic options, and we will work with families to find financial solutions to make this possible.

Getting started is simple and free. You share your genetic data with us, and our team analyzes whether a custom therapy might be appropriate for your condition. We share this information directly with you via an emailed report. We are available to help explain next steps and meet with your clinical care team as appropriate. There's no cost for the initial assessment and you decide whether you want to proceed to subsequent steps with no obligation to do so.