You’re not alone on your rare disease journey
Nome transforms complex genetic pictures into clear, actionable roadmaps that can guide you to treatments.
You want options that are built for your unique condition.
So do we. Let’s see what’s possible.
How Nome Works
Nome brings together proven science, technology and a network of experts to develop experimental treatments for rare inherited genetic diseases.
Start your journey
Share your diagnosis
Summary Report
AI generated, expert reviewed. Your free evaluation of custom therapy options.
Engage with our team
Receive live follow-up support to dig deeper into what’s possible.
Action Plan
Execution ready, highly detailed next steps tailored to you.
Ongoing Support
We’re here every step of the way.
Who We Help
Nome supports those affected by rare genetic conditions and the healthcare professionals working to build treatments. We are focused on inherited diseases, not cancer, at this time.
Rare Disease Patients, Parents & Families
Clear guidance around the drug development process, specifically whether an experimental therapy could change the trajectory of your disease
Clinicians
A secure, trusted platform to find emerging experimental therapies that could help patients
Research Labs
Access to technology, data and patients that can optimize clinical research activities and accelerate discovery
Pharmaceutical Companies
Validation of the business case for platform treatment opportunities that can treat multiple rare conditions
Take the First Step
Your journey to potential treatments starts today.