You’re not alone on your rare disease journey

Nome transforms complex genetic pictures into clear, actionable roadmaps that can guide you to treatments.

You want options that are built for your unique condition. 

So do we. Let’s see what’s possible.

What we do: provide genetic medicine development as a service for rare disease families, foundations, and health systems

Nome is a services company that helps rare disease families, patient foundations, and health systems access and develop personalized genetic medicines. We work across the full lifecycle of a therapeutic program — from diagnosis to treatment design to clinical execution — using an AI platform combined with human experts to make this process faster, lower-cost, and more accessible than traditional drug development. For families and organizations navigating the emerging world of n-of-1 and rare disease genetic therapies, we are the 'easy button' that provides concierge navigation through this process. Nome is the operating system for personalized therapies.™

How Nome Works

Nome brings together proven science, technology and a network of experts to develop experimental treatments for rare inherited genetic diseases. 

Step 1

Start your journey

Initial assessment icon — Nome evaluates your child's genetic diagnosis

Share your diagnosis


Summary Report

Step 2
Expert review icon — specialists analyze treatment options

AI generated, expert reviewed. Your free evaluation of custom therapy options.


Engage with our team

Receive live follow-up support to dig deeper into what’s possible.

Summary report icon — receive a personalized treatment roadmap

Action Plan

Execution ready, highly detailed next steps tailored to you.

Action plan icon — clear next steps for pursuing therapy

Ongoing Support

We’re here every step of the way.

Ongoing support icon — Nome guides you through the entire process

Who We Help

Nome supports those affected by rare genetic conditions and the healthcare professionals working to build treatments. We are focused on inherited diseases, not cancer, at this time.

Patients and families — personalized rare disease therapy guidance

Rare Disease Patients, Parents & Families

Clear guidance around the drug development process, specifically whether an experimental therapy could change the trajectory of your disease


Healthcare provideClinicians — partner with Nome for patient treatment optionsrs icon

Clinicians

A secure, trusted platform to find emerging experimental therapies that could help patients


Research laboratories — collaborate on rare disease therapeutics

Research Labs

Access to technology, data and patients that can optimize clinical research activities and accelerate discovery


Pharmaceutical companies — rare disease drug development partnerships

Pharmaceutical Companies

Validation of the business case for platform treatment opportunities that can treat multiple rare conditions


Take the First Step

Your journey to potential treatments starts today.