Blog

Discover the latest updates from Nome Therapeutics — exploring rare disease research, scientific breakthroughs, and innovations in personalized therapies.

ABCD1 Gene Disorders: Research Update and Personalized ASO Therapy Options

Nome Team 10/29/25 Nome Team 10/29/25

ABCD1 Gene Disorders: Research Update and Personalized ASO Therapy Options

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GBA Gene Disorders: Research Update and Personalized ASO Therapy Options

Nome Team 10/29/25 Nome Team 10/29/25

GBA Gene Disorders: Research Update and Personalized ASO Therapy Options

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PSEN1 Gene Disorders: Research Update and Personalized ASO Therapy Options

Nome Team 10/29/25 Nome Team 10/29/25

PSEN1 Gene Disorders: Research Update and Personalized ASO Therapy Options

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SCN1A Gene Disorders: Research Update and Personalized ASO Therapy Options

Nome Team 10/29/25 Nome Team 10/29/25

SCN1A Gene Disorders: Research Update and Personalized ASO Therapy Options

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ATM Gene Disorders: Research Update and Personalized ASO Therapy Options

Nome Team 10/29/25 Nome Team 10/29/25

ATM Gene Disorders: Research Update and Personalized ASO Therapy Options

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SMN1 Gene Disorders: Research Update and Personalized ASO Therapy Options

Nome Team 10/29/25 Nome Team 10/29/25

SMN1 Gene Disorders: Research Update and Personalized ASO Therapy Options

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List of Hospitals and Doctors Helping with APOE Disorders in California

Nome Team 10/23/25 Nome Team 10/23/25

List of Hospitals and Doctors Helping with APOE Disorders in California

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List of Resources For Rare Disease Patients In Texas

Nome Team 10/23/25 Nome Team 10/23/25

List of Resources For Rare Disease Patients In Texas

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APOE Disorders: 10 Organizations, 12 Technologies, and Clinical Trials Every Family Should Know

Nome Team 10/23/25 Nome Team 10/23/25

APOE Disorders: 10 Organizations, 12 Technologies, and Clinical Trials Every Family Should Know

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How mRNA Therapy Helps with Genetic Disorders

Nome Team 10/23/25 Nome Team 10/23/25

How mRNA Therapy Helps with Genetic Disorders

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12 Leading Experts Advancing Cystic Fibrosis Gene Therapy

Nome Team 10/23/25 Nome Team 10/23/25

12 Leading Experts Advancing Cystic Fibrosis Gene Therapy

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12 Leading Experts Advancing Sickle Cell Disease Gene Therapy

Nome Team 10/23/25 Nome Team 10/23/25

12 Leading Experts Advancing Sickle Cell Disease Gene Therapy

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Rare Disease Statistics: 38 Key Data Points Every Healthcare Leader Should Know in 2025

Nome Team 10/23/25 Nome Team 10/23/25

Rare Disease Statistics: 38 Key Data Points Every Healthcare Leader Should Know in 2025

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APOE Gene Disorders: Research Update and Personalized ASO Therapy Options

Nome Team 10/23/25 Nome Team 10/23/25

APOE Gene Disorders: Research Update and Personalized ASO Therapy Options

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9 California Hospitals and 12 Specialists Treating KCNT1 Epilepsy (Plus How Nome Delivers Personalized ASO Therapy)

Nome Team 10/23/25 Nome Team 10/23/25

9 California Hospitals and 12 Specialists Treating KCNT1 Epilepsy (Plus How Nome Delivers Personalized ASO Therapy)

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15 Leading Experts Advancing N-of-1 ASO Treatment for Rare Diseases

Nome Team 10/23/25 Nome Team 10/23/25

15 Leading Experts Advancing N-of-1 ASO Treatment for Rare Diseases

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How CRISPR Helps with Genetic Disorders

Nome Team 10/23/25 Nome Team 10/23/25

How CRISPR Helps with Genetic Disorders

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AIMP2 Gene Disorders: Research Update and Personalized ASO Therapy Options

Nome Team 10/22/25 Nome Team 10/22/25

AIMP2 Gene Disorders: Research Update and Personalized ASO Therapy Options

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Personalized Medicine Strategies for SCN2A-Related Disorders

Nome Team 10/22/25 Nome Team 10/22/25

Personalized Medicine Strategies for SCN2A-Related Disorders

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KCNT1 Epilepsy Resource Guide

Nome Team 10/21/25 Nome Team 10/21/25

KCNT1 Epilepsy Resource Guide

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